Society for Medical Decision Making (SMDM) 2022
Item-Level Findings and Longitudinal Fatigue Scores Among Patients with Paroxysmal Nocturnal Hemoglobinuria from the Phase 3 PRINCE Study
FACIT-Fatigue Responders and Related Hemoglobin Improvements After Pegcetacoplan in Treatment Naïve Patients with Paroxysmal Nocturnal Hemoglobinuria