National Organization for Rare Disorders (NORD) 2022

Hemoglobin, Lactate Dehydrogenase, and FACIT-Fatigue Normalization in Pegcetacoplan-treated Patients with Paroxysmal Nocturnal Hemoglobinuria

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Normalization of Hematologic Markers and Fatigue in Patients with Paroxysmal Nocturnal Hemoglobinuria Treated with Pegcetacoplan and Baseline Hemoglobin at or Above 10 g/dL

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