International AAMDSIF Bone Marrow Failure Disease Scientific Symposium (AAMDSIF BMF) 2024
Efficacy and Safety Is Maintained in Adult Patients With Paroxysmal Nocturnal Hemoglobinuria Receiving Pegcetacoplan for Up to 3 Years
Human Factors Validation Study for a Wearable, Single-Use Injector and a User Experience Survey of Complement Inhibitor-Treated Patients with Paroxysmal Nocturnal Hemoglobinuria
Improvement in Iron Overload With Pegcetacoplan Therapy in Patients With Paroxysmal Nocturnal Hemoglobinuria Previously Treated With Eculizumab