The European Society for Blood and Marrow Transplantation (EBMT) 2021
Clinical Burden of Illness Survey Results for U.S. Patients with Paroxysmal Nocturnal Hemoglobinuria Receiving C5 Inhibitors
Improvements in Fatigue and Physical Function Evaluated Through Changes in Clinical Outcomes in Paroxysmal Nocturnal Hemoglobinuria: Post-Hoc Analyses from the PEGASUS Study
Injection-Site Reactions in the Randomized Phase 3 PEGASUS Trial of Pegcetacoplan Compared With Eculizumab for Individuals With Paroxysmal Nocturnal Hemoglobinuria
Work Productivity Loss and Quality of Life in Paroxysmal Nocturnal Hemoglobinuria Among Patients Receiving C5 Inhibitors in the United States