The European Society for Blood and Marrow Transplantation (EBMT) 2021

Clinical Burden of Illness Survey Results for U.S. Patients with Paroxysmal Nocturnal Hemoglobinuria Receiving C5 Inhibitors

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Improvements in Fatigue and Physical Function Evaluated Through Changes in Clinical Outcomes in Paroxysmal Nocturnal Hemoglobinuria: Post-Hoc Analyses from the PEGASUS Study

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Injection-Site Reactions in the Randomized Phase 3 PEGASUS Trial of Pegcetacoplan Compared With Eculizumab for Individuals With Paroxysmal Nocturnal Hemoglobinuria

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Work Productivity Loss and Quality of Life in Paroxysmal Nocturnal Hemoglobinuria Among Patients Receiving C5 Inhibitors in the United States

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